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    [{"orgOrder":0,"company":"BridgeBio Pharma","sponsor":"Sentynl Therapeutics","pharmaFlowCategory":"D","therapeuticArea":"Genetic Disease","country":"U.S.A","productType":"Other Small Molecule","year":"2022","type":"Agreement","leadProduct":"Fosdenopterin","moa":"cPMP","graph1":"Genetic Disease","graph2":"Approved FDF","graph3":"BridgeBio Pharma","amount2":0,"highestDevelopmentShortName":"","therapeuticAreaShortName":"Genetic Disease","amount2New":0,"dosageForm":"Intravenous Injection","sponsorNew":"BridgeBio Pharma \/ Sentynl Therapeutics","highestDevelopmentStatusID":"15","companyTruncated":"BridgeBio Pharma \/ Sentynl Therapeutics"},{"orgOrder":0,"company":"BridgeBio Pharma","sponsor":"Sentynl Therapeutics","pharmaFlowCategory":"DU","therapeuticArea":"Genetic Disease","country":"U.S.A","productType":"Other Small Molecule","year":"2022","type":"Inapplicable","leadProduct":"Fosdenopterin","moa":"cPMP","graph1":"Genetic Disease","graph2":"Approved FDF","graph3":"BridgeBio Pharma","amount2":0,"highestDevelopmentShortName":"","therapeuticAreaShortName":"Genetic Disease","amount2New":0,"dosageForm":"Intravenous Injection","sponsorNew":"BridgeBio Pharma \/ Sentynl Therapeutics","highestDevelopmentStatusID":"15","companyTruncated":"BridgeBio Pharma \/ Sentynl Therapeutics"},{"orgOrder":0,"company":"BridgeBio Pharma","sponsor":"Inapplicable","pharmaFlowCategory":"DU","therapeuticArea":"Genetic Disease","country":"U.S.A","productType":"Other Small Molecule","year":"2020","type":"Inapplicable","leadProduct":"Fosdenopterin","moa":"cPMP","graph1":"Genetic Disease","graph2":"Approved FDF","graph3":"BridgeBio Pharma","amount2":0,"highestDevelopmentShortName":"","therapeuticAreaShortName":"Genetic Disease","amount2New":0,"dosageForm":"Intravenous Injection","sponsorNew":"BridgeBio Pharma \/ Inapplicable","highestDevelopmentStatusID":"15","companyTruncated":"BridgeBio Pharma \/ Inapplicable"},{"orgOrder":0,"company":"BridgeBio Pharma","sponsor":"Sentynl Therapeutics","pharmaFlowCategory":"DU","therapeuticArea":"Genetic Disease","country":"U.S.A","productType":"Other Small Molecule","year":"2022","type":"Inapplicable","leadProduct":"Fosdenopterin","moa":"cPMP","graph1":"Genetic Disease","graph2":"Approved FDF","graph3":"BridgeBio Pharma","amount2":0,"highestDevelopmentShortName":"","therapeuticAreaShortName":"Genetic Disease","amount2New":0,"dosageForm":"Intravenous Injection","sponsorNew":"BridgeBio Pharma \/ Sentynl Therapeutics","highestDevelopmentStatusID":"15","companyTruncated":"BridgeBio Pharma \/ Sentynl Therapeutics"},{"orgOrder":0,"company":"BridgeBio Pharma","sponsor":"Sentynl Therapeutics","pharmaFlowCategory":"DU","therapeuticArea":"Genetic Disease","country":"U.S.A","productType":"Other Small Molecule","year":"2022","type":"Inapplicable","leadProduct":"Fosdenopterin","moa":"cPMP","graph1":"Genetic Disease","graph2":"Approved FDF","graph3":"BridgeBio Pharma","amount2":0,"highestDevelopmentShortName":"","therapeuticAreaShortName":"Genetic Disease","amount2New":0,"dosageForm":"Intravenous Injection","sponsorNew":"BridgeBio Pharma \/ Sentynl Therapeutics","highestDevelopmentStatusID":"15","companyTruncated":"BridgeBio Pharma \/ Sentynl Therapeutics"},{"orgOrder":0,"company":"Sentynl Therapeutics","sponsor":"Inapplicable","pharmaFlowCategory":"DU","therapeuticArea":"Rare Diseases and Disorders","country":"U.S.A","productType":"Other Small Molecule","year":"2024","type":"Inapplicable","leadProduct":"Fosdenopterin","moa":"cPMP","graph1":"Rare Diseases and Disorders","graph2":"Approved FDF","graph3":"Sentynl Therapeutics","amount2":0,"highestDevelopmentShortName":"","therapeuticAreaShortName":"Rare Diseases","amount2New":0,"dosageForm":"Intravenous Infusion","sponsorNew":"Sentynl Therapeutics \/ Inapplicable","highestDevelopmentStatusID":"15","companyTruncated":"Sentynl Therapeutics \/ Inapplicable"},{"orgOrder":0,"company":"BridgeBio Pharma","sponsor":"Inapplicable","pharmaFlowCategory":"DU","therapeuticArea":"Genetic Disease","country":"U.S.A","productType":"Other Small Molecule","year":"2021","type":"Inapplicable","leadProduct":"Fosdenopterin","moa":"cPMP","graph1":"Genetic Disease","graph2":"Approved FDF","graph3":"BridgeBio Pharma","amount2":0,"highestDevelopmentShortName":"","therapeuticAreaShortName":"Genetic Disease","amount2New":0,"dosageForm":"Intravenous Injection","sponsorNew":"BridgeBio Pharma \/ Inapplicable","highestDevelopmentStatusID":"15","companyTruncated":"BridgeBio Pharma \/ Inapplicable"}]

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    Sentynl Therapeutics

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    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Rare Diseases and Disorders

    Study Phase : Approved FDF

    Sponsor : Inapplicable

    Deal Size : Inapplicable

    Deal Type : Inapplicable

    DEALS_DEV arrow-down

    Sentynl Receives MHRA Authorization for NULIBRY® in MoCD Type A

    Details : Nulibry (fosdenopterin) is the first therapy for patients in Great Britain with molybdenum cofactor deficiency Type A, an ultra-rare genetic disorder that often progresses rapidly in infants.

    Product Name : Nulibry

    Product Type : Other Small Molecule

    Upfront Cash : Inapplicable

    April 16, 2024

    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Rare Diseases and Disorders

    Highest Development Status : Approved FDF

    Sponsor : Inapplicable

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    BridgeBio Pharma

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    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Study Phase : Approved FDF

    Sponsor : Sentynl Therapeutics

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    BridgeBio Pharma, Sentynl Therapeutics and Medison Pharma Announce Approval in Israel for NULIBRY® (fosdenopt...

    Details : NULIBRY (fosdenopterin) is first and only approved therapy in U.S. and in Israel to treat patients with MoCD Type A, an ultra-rare, life-threatening genetic disorder that often progresses rapidly in infants with a median overall survival age of about fou...

    Product Name : Nulibry

    Product Type : Other Small Molecule

    Upfront Cash : Inapplicable

    October 08, 2022

    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Highest Development Status : Approved FDF

    Sponsor : Sentynl Therapeutics

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    BridgeBio Pharma

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    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Study Phase : Approved FDF

    Sponsor : Sentynl Therapeutics

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    BridgeBio Pharma and Sentynl Therapeutics Receive Marketing Authorization in the EU for NULIBRY® (fosdenopter...

    Details : Nulibry (fosdenopterin) is a first-in-class cPMP substrate replacement therapy that was approved by the U.S. Food and Drug Administration (FDA) in 2021 to reduce the risk of mortality in patients with MoCD Type A.

    Product Name : Nulibry

    Product Type : Other Small Molecule

    Upfront Cash : Inapplicable

    September 20, 2022

    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Highest Development Status : Approved FDF

    Sponsor : Sentynl Therapeutics

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    BridgeBio Pharma

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    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Study Phase : Approved FDF

    Sponsor : Sentynl Therapeutics

    Deal Size : Undisclosed

    Deal Type : Agreement

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    BridgeBio Pharma and Sentynl Therapeutics Announce Asset Purchase Agreement for BridgeBio Pharma’s NULIBRY�...

    Details : Under the Agreement, Sentynl will acquire global rights to NULIBRY and will be responsible for the ongoing development and commercialization of NULIBRY in the United States and developing, manufacturing and commercializing Fosdenopterin globally.

    Product Name : Nulibry

    Product Type : Other Small Molecule

    Upfront Cash : Undisclosed

    August 03, 2022

    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Highest Development Status : Approved FDF

    Sponsor : Sentynl Therapeutics

    Deal Size : Undisclosed

    Deal Type : Agreement

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    BridgeBio Pharma

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    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Study Phase : Approved FDF

    Sponsor : Sentynl Therapeutics

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    BridgeBio Pharma and Sentynl Therapeutics Receive Positive CHMP Opinion for NULIBRY (fosdenopterin) for the Tr...

    Details : CHMP recommendation for approval of NULIBRY (fosdenopterin) in European Union (EU) for the treatment of patients with molybdenum cofactor deficiency (MoCD) Type A is based on the efficacy and safety data collected to date compared to data from a natural ...

    Product Name : Nulibry

    Product Type : Other Small Molecule

    Upfront Cash : Inapplicable

    July 25, 2022

    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Highest Development Status : Approved FDF

    Sponsor : Sentynl Therapeutics

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Study Phase : Approved FDF

    Sponsor : Inapplicable

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    Bridgebio Pharma and Affiliate Origin Biosciences Announce fda Approval of Nulibry

    Details : The efficacy of NULIBRY for the treatment of patients with MoCD Type A was established based on data from three clinical trials compared to data from a natural history study in which it showed a meaningful increase in overall survival compared to a natur...

    Product Name : Nulibry

    Product Type : Other Small Molecule

    Upfront Cash : Inapplicable

    February 28, 2021

    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Highest Development Status : Approved FDF

    Sponsor : Inapplicable

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    BridgeBio Pharma

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    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Study Phase : Phase III

    Sponsor : Inapplicable

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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    BridgeBio Pharma and Origin Biosciences Gets FDA Acceptance Of Its New Drug Application For Fosdenopterin For ...

    Details : FDA has accepted its New Drug Application (NDA) for fosdenopterin, a cyclic pyranopterin monophosphate (cPMP) substrate replacement therapy, for the treatment of patients with molybdenum cofactor deficiency (MoCD) Type A.

    Product Name : Nulibry

    Product Type : Other Small Molecule

    Upfront Cash : Inapplicable

    September 29, 2020

    Lead Product(s) : Fosdenopterin

    Therapeutic Area : Genetic Disease

    Highest Development Status : Phase III

    Sponsor : Inapplicable

    Deal Size : Inapplicable

    Deal Type : Inapplicable

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