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The partnership aims to discover and provide personalized experimental antisense oligonucleotide medicines to nano-rare disease patients. Hongene will provide amidites, compounds essential to developing ASO medicines, to n-Lorem to offset the costs of developing ASO medicines.
Lead Product(s): ASO-based Therapy
Therapeutic Area: Rare Diseases and Disorders Product Name: Undiclosed
Highest Development Status: Discovery Product Type: Large molecule
Partner/Sponsor/Collaborator: n-Lorem Foundation
Deal Size: Undisclosed Upfront Cash: Undisclosed
Deal Type: Partnership April 24, 2024