Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : ASO-based Therapy
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery Platform
Recipient : Hongene Biotech
Deal Size : Undisclosed
Deal Type : Partnership
n-Lorem Partners with Hongene for Personalized ASO Medicines
Details : The partnership will discover personalized antisense oligonucleotide medicines for nano-rare disease patients, with Hongene providing essential compounds to n-Lorem to offset development costs.
Brand Name : Undiclosed
Molecule Type : Large molecule
Upfront Cash : Undisclosed
April 24, 2024
Lead Product(s) : ASO-based Therapy
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery Platform
Recipient : Hongene Biotech
Deal Size : Undisclosed
Deal Type : Partnership
Lead Product(s) : Antisense Oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Recipient : St. Jude Children’s Research Hospital
Deal Size : Undisclosed
Deal Type : Collaboration
n-Lorem Foundation Collaborates to Support Children With Extremely Rare Diseases
Details : The collaboration aims to accelerate the development of optimized experimental antisense oligonucleotide (ASO) medicines for pediatric patients with extremely rare genetic neurological disorders.
Brand Name : Undisclosed
Molecule Type : Large molecule
Upfront Cash : Undisclosed
October 04, 2023
Lead Product(s) : Antisense Oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Recipient : St. Jude Children’s Research Hospital
Deal Size : Undisclosed
Deal Type : Collaboration
Lead Product(s) : Antisense Oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Sponsor : The Conrad Prebys Foundation
Deal Size : $0.3 million
Deal Type : Funding
Details : The funding will support n-Lorem’s efforts to discover optimal ASO candidates for several nano-rare patients. Once identified, n-Lorem will conduct preclinical studies necessary to support clinical development for each optimized ASO.
Brand Name : Undisclosed
Molecule Type : Large molecule
Upfront Cash : Undisclosed
March 21, 2022
Lead Product(s) : Antisense Oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Sponsor : The Conrad Prebys Foundation
Deal Size : $0.3 million
Deal Type : Funding
Lead Product(s) : Antisense Oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Recipient : Parexel Biotech
Deal Size : Undisclosed
Deal Type : Partnership
Details : Partnership will support the n-Lorem’s effort to discover and provide experimental antisense oligonucleotide (ASO) medicines to nano-rare disease patients (1 to 30 patients worldwide) for free, for life.
Brand Name : Undisclosed
Molecule Type : Large molecule
Upfront Cash : Undisclosed
February 23, 2022
Lead Product(s) : Antisense Oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Recipient : Parexel Biotech
Deal Size : Undisclosed
Deal Type : Partnership
Lead Product(s) : Antisense Oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Recipient : Cytiva
Deal Size : Undisclosed
Deal Type : Partnership
Details : The collaboration aim to discover and provide experimental antisense oligonucleotide (ASO) medicines to nano-rare disease patients (1 to 30 patients worldwide) for free, for life.
Brand Name : Undisclosed
Molecule Type : Large molecule
Upfront Cash : Undisclosed
February 08, 2022
Lead Product(s) : Antisense Oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Recipient : Cytiva
Deal Size : Undisclosed
Deal Type : Partnership
Lead Product(s) : Antisense Oligonucleotides
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Undisclosed
Recipient : Argonaut Manufacturing Services
Deal Size : Undisclosed
Deal Type : Partnership
Details : The partnership will supports and reduces the cost of manufacturing of n-Lorem’s experimental antisense oligonucleotide (ASO) medicines developed for nano-rare disease patients (1 to 30 patients worldwide) for free, for life.
Brand Name : Undisclosed
Molecule Type : Large molecule
Upfront Cash : Undisclosed
February 02, 2022
Lead Product(s) : Antisense Oligonucleotides
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Undisclosed
Recipient : Argonaut Manufacturing Services
Deal Size : Undisclosed
Deal Type : Partnership
Lead Product(s) : Antisense oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Discovery
Recipient : Ultragenyx Pharmaceutical
Deal Size : Undisclosed
Deal Type : Collaboration
Details : n-Lorem Foundation is the first and only foundation with a mission to provide potentially life-saving treatments to patients who have diseases caused by extremely rare mutations for free by coupling advanced genomic diagnostics with antisense oligonucleo...
Brand Name : Undisclosed
Molecule Type : Large molecule
Upfront Cash : Undisclosed
April 05, 2021
Lead Product(s) : Antisense oligonucleotide
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Discovery
Recipient : Ultragenyx Pharmaceutical
Deal Size : Undisclosed
Deal Type : Collaboration
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