Year
DEALS // DEV.
Country
Therapeutic Area
Study Phase
Deal Type
Product Type
Dosage Form
Lead Product
Target
Lead Product(s) : GEN6050X
Therapeutic Area : Genetic Disease
Study Phase : IND Enabling
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
GenAssist’s GEN6050X IND Cleared by FDA for Duchenne Muscular Dystrophy
Details : GEN6050X, a globally first-in-class base editing drug, which is currently being evaluated for the treatment of duchenne muscular dystrophy.
Product Name : GEN6050X
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
March 06, 2025
Lead Product(s) : GEN6050X
Therapeutic Area : Genetic Disease
Highest Development Status : IND Enabling
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Lead Product(s) : GEN6050
Therapeutic Area : Genetic Disease
Study Phase : IND Enabling
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable
Details : GEN6050 is an in vivo base editing drug that targets exon 50 skipping in the Duchenne muscular dystrophy (DMD) gene. It is designed to restore the expression of dystrophin protein by base editing.
Product Name : GEN6050
Product Type : Cell and Gene therapy
Upfront Cash : Inapplicable
June 05, 2023
Lead Product(s) : GEN6050
Therapeutic Area : Genetic Disease
Highest Development Status : IND Enabling
Sponsor : Inapplicable
Deal Size : Inapplicable
Deal Type : Inapplicable