3
ALL3
TheranexusYear
3
ALL1
20241
20231
2020DEALS // DEV.
3
ALL1
Deals2
DevelopmentsCountry
2
ALL2
FRANCE3
ALL1
Beyond Batten Disease Foundation1
Exelixis1
Not ApplicableTherapeutic Area
3
ALL1
Genetic Disease1
Neurology1
Rare Diseases and DisordersStudy Phase
3
ALL1
Phase III1
Phase I1
PreclinicalDeal Type
1
ALL1
Licensing AgreementProduct Type
3
ALL2
Small molecule1
UndisclosedDosage Form
2
ALL2
CapsuleLead Product
3
ALL1
Donepezil1
Miglustat1
TX01Target
1
ALL1
AchELead Product(s) : TX01
Therapeutic Area : Rare Diseases and Disorders
Study Phase : Preclinical
Sponsor : Exelixis
Deal Size : Undisclosed
Deal Type : Licensing Agreement
Theranexus and Exeltis License Tx01 for Two Rare Neurological Disorders
Details : Under the licensing agreement, Exeltis will acquire exclusive rights to market and distribute Theranexus' proprietary product TX01 for treating Gaucher & Niemann-Pick Disease Type C.
Product Name : 2.1
Product Type : Undisclosed
Upfront Cash : $2.1 million
December 17, 2024
Lead Product(s) : TX01
Therapeutic Area : Rare Diseases and Disorders
Highest Development Status : Preclinical
Sponsor : Exelixis
Deal Size : Undisclosed
Deal Type : Licensing Agreement
Lead Product(s) : Miglustat
Therapeutic Area : Genetic Disease
Study Phase : Phase III
Sponsor : Beyond Batten Disease Foundation
Deal Size : Not Applicable
Deal Type : Not Applicable
Details : Batten-1 is a novel and exclusive proprietary drug containing the active ingredient miglustat. The mechanism of action of this substance blocks the accumulation of glycosphingolipids and neuroinflammation. It is being investigated for CLN3 batten disease...
Product Name : Batten-1
Product Type : Small molecule
Upfront Cash : Not Applicable
May 09, 2023
Lead Product(s) : Miglustat
Therapeutic Area : Genetic Disease
Highest Development Status : Phase III
Sponsor : Beyond Batten Disease Foundation
Deal Size : Not Applicable
Deal Type : Not Applicable
Lead Product(s) : Donepezil,Mefloquine
Therapeutic Area : Neurology
Study Phase : Phase I
Sponsor : Not Applicable
Deal Size : Not Applicable
Deal Type : Not Applicable
Details : THN201 significantly increased EEG power in the gamma band related to cognitive activity. Similar profile with respect to other pharmacological, pharmacokinetic and tolerance endpoints was observed.
Product Name : Undisclosed
Product Type : Small molecule
Upfront Cash : Not Applicable
January 15, 2020
Lead Product(s) : Donepezil,Mefloquine
Therapeutic Area : Neurology
Highest Development Status : Phase I
Sponsor : Not Applicable
Deal Size : Not Applicable
Deal Type : Not Applicable