[{"orgOrder":0,"company":"PTC Therapeutics","sponsor":"Novartis Pharmaceuticals Corporation","pharmaFlowCategory":"D","therapeuticArea":"Genetic Disease","country":"","productType":"Small molecule","year":"2024","type":"Licensing Agreement","leadProduct":"Votoplam","moa":"","graph1":"Genetic Disease","graph2":"Phase II","graph3":"PTC Therapeutics","amount2":2.8999999999999999,"highestDevelopmentShortName":"Ph II","therapeuticAreaShortName":"Genetic Disease","amount2New":2.8999999999999999,"dosageForm":"","sponsorNew":"PTC Therapeutics \/ Novartis Pharmaceuticals Corporation","highestDevelopmentStatusID":"8","companyTruncated":"PTC Therapeutics \/ Novartis Pharmaceuticals Corporation"}]

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                          PharmScience R&D
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                          PharmScience R&D
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                          Details : Under the licensing agreement, Novartis will assume responsibility for PTC518 (Votoplam) development, manufacturing and commercialization for the treatment of Huntington's disease.

                          Product Name : PTC518

                          Product Type : Small molecule

                          Upfront Cash : $1,000.0 million

                          December 02, 2024

                          Lead Product(s) : Votoplam

                          Therapeutic Area : Genetic Disease

                          Highest Development Status : Phase II

                          Sponsor : Novartis Pharmaceuticals Corporation

                          Deal Size : $2,900.0 million

                          Deal Type : Licensing Agreement

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